Molecular diseases (genetic disorders) are non-infectious inheritable diseases which are usually caused by mutations that […]
Category: Gene Therapy Notes
POTENTIAL USES OF GENE THERAPY
Gene therapy techniques are an emerging field of experimental medicine and therapy for treating or […]
HOW GENE THERAPY WORKS
Genes are made of deoxyribonucleic acid (DNA) molecules – which are the main genetic material […]
EX VIVO DELIVERY FOR GENE THERAPY
Ex vivo delivery can also be called cell-based delivery protocol of gene therapy. It is […]
IN VIVO DELIVERY FOR GENE THERAPY
In vivo delivery for gene therapy can also be called a direct delivery protocol for […]
PLASMIDS
Plasmids are extrachromosomal DNA molecules found in both eukaryotic and prokaryotic microorganisms that have the […]
GENE THERAPY TARGETING AND DELIVERY
The efficient delivery of therapeutic proteins or DNA into specific cells or tissues of an […]
PREREQUISITES OR STEPS FOR GENE THERAPY
Gene therapy is an experimental discipline or research that uses functional gene (i.e. therapeutic DNA) […]
HISTORY OF GENE THERAPY
The history of gene therapy techniques dates back to the early 1970s and 1980s when […]
GENE THERAPY
Gene therapy is defined as the specific genetic manipulation and modification of an organism’s genome […]
NITROGENOUS BASES – Purine and Pyrimidines
Genes in the DNA code for proteins; and it is the gene that directs the […]
Genes
Genes are sections of the deoxyribonucleic acid (DNA) that codes for the synthesis of a […]
FDA Approves First Gene Therapies to Treat Patients with Sickle Cell Disease
Today, the U.S. Food and Drug Administration approved two milestone treatments, Casgevy and Lyfgenia, representing […]